Adeno-associated virus vectors (AAV) show promise for liver-targeted gene therapy. imaging and histologic follow-up of this large cohort of NHP exposed no toxicity. These data support further evaluation of this vector in hemophilia B individuals. PIK3C3 Intro Hemophilia B an X-linked bleeding disorder is definitely ideally suited for gene alternative methods. This is partly because… Continue reading Adeno-associated virus vectors (AAV) show promise for liver-targeted gene therapy. imaging